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A Breakthrough for MCT8 Deficiency: FDA Approves Emcitate (tiratricol)
A Milestone in Rare Disease Treatment For patients and families living with MCT8 deficiency, a significant milestone has been reached. The U.S. Food and Drug Administration (FDA) has officially approved Emcitate (tiratricol), marking a transformative step forward in the treatment of this ultra-rare thyroid hormone transport disorder. Understanding MCT8 Deficiency MCT8 deficiency is a rare…